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Report
Tay-Sachs Disease Market Report and Forecast 2024-2032
Market Report (7 days) I 2024-02-12 I 180 Pages I EMR Inc.
Tay Sachs Disease Market Report and Forecast 2024-2032
Tay Sachs Disease Market Outlook
The Tay Sachs disease market size was valued at USD 2.1 billion in 2023, driven by the increasing investment to development effective treatment alternatives across the major markets. The market size is anticipated to grow at a CAGR of 5.6% during the forecast period of 2024-2032 to achieve a value of USD 3.4 billion by 2032.
Tay Sachs Disease: Introduction
Tay-Sachs disease is a rare, inherited neurodegenerative disorder. It's caused by the absence of a vital enzyme, hexosaminidase A, leading to the accumulation of a fatty substance (GM2 ganglioside) in nerve cells in the brain and spinal cord. This accumulation progressively destroys nerve cells, affecting mental and physical abilities. Symptoms, appearing in infancy, include muscle weakness, motor skill regression, and severe neurological impairment. Currently, there's no cure, with treatment focusing on managing symptoms and providing supportive care.
Key Trends in the Tay Sachs Disease Market
Significant investment in research is focused on understanding the genetic and biochemical basis of Tay-Sachs disease to develop potential therapies. Clinical trials are exploring gene therapy, enzyme replacement therapies, and substrate reduction therapies as potential treatments.
Many regions have implemented or are advocating for newborn screening programs to detect Tay-Sachs disease early. Early diagnosis allows for prompt intervention and management, even though options are currently limited to supportive care.
As Tay-Sachs is a progressive, debilitating condition, there's a focus on improving the quality of life of patients and families. This includes advancements in palliative care, physical therapy, and nutritional support, as well as services to assist families in managing the emotional and practical challenges of the disease.
With Tay-Sachs being an inheritable condition, genetic counseling services are essential. They provide families and prospective parents with information about the risks, enabling informed decisions regarding family planning and the management of the condition if diagnosed.
The rarity of Tay-Sachs disease necessitates global collaboration for research, funding, and sharing of knowledge. Networks and alliances among research institutions, healthcare providers, and patient advocacy groups are crucial in driving advancements in understanding and managing the disease.
Tay Sachs Disease Market Segmentation
Market Breakup by Drug Type
- Anticonvulsants
- Antipsychotic Medications
- Others
Market Breakup by Type
- Infantile Tay - Sachs Disease
- Juvenile Tay-Sachs Disease
- Late-Onset Tay-Sachs Disease
Market Breakup by Treatment
- Medication
- Respiratory Care
- Physical Therapy
Market Breakup by Route of Administration
- Injectable
- Oral
- Others
Market Breakup by Distribution Channel
- Hospital Pharmacies
- Retail Pharmacies
- Online Pharmacies
Market Breakup by End User
- Hospitals
- Homecare
Market Breakup by Region
- United States
- EU-4 and the United Kingdom
o Germany
o France
o Italy
o Spain
o United Kingdom
- Japan
Tay Sachs Disease Market Overview
In North America, the Tay-Sachs disease market is primarily focused on supportive care and research for potential treatments due to the condition's rarity and severity. The region has strong patient advocacy groups that provide resources and support to affected families. Research efforts are significant, with a focus on gene therapy, enzyme replacement therapies, and other innovative approaches. The market is also influenced by screening programs, particularly within communities with higher prevalence rates, to identify carriers and provide genetic counseling.
Europe's market benefits from well-established healthcare systems and comprehensive support for rare disease research and treatment. The European Union has initiatives to encourage the development of treatments for rare diseases, including Tay-Sachs. Collaborative research efforts across countries focus on understanding the disease mechanism and exploring potential therapies. Newborn screening and genetic counseling services are integral parts of the healthcare approach, aiming to manage the disease's impact and support affected families.
Japan's market for Tay-Sachs disease is characterized by advanced healthcare research and a commitment to addressing rare diseases. The country focuses on innovative medical research and healthcare solutions, including the exploration of potential treatments for Tay-Sachs. Supportive care and services for affected individuals and families are important aspects of the market. Japan's approach to rare diseases also includes efforts in early diagnosis, public awareness, and providing access to specialized healthcare services.
Tay Sachs Disease Market: Competitor Landscape
The key features of the market report include patent analysis, grants analysis, clinical trials analysis, funding and investment analysis, partnerships, and collaborations analysis by the leading key players.
- Recursion Pharmaceuticals, Inc.
- IntraBioInc
- Johnson & Johnson Services
- Axovant Sciences, Inc.
- Pfizer
- Sio Gene Therapies Ltd
- F. Hoffmann-La
- Roche Ltd
- Bayer AG
- Bausch Health
- Boehringer Ingelheim International GmbH
We at Expert Market Research always strive to provide you with the latest information. The numbers in the article are only indicative and may be different from the actual report.
1 Preface
1.1 Objectives of the Study
1.2 Key Assumptions
1.3 Report Coverage - Key Segmentation and Scope
1.4 Research Methodology
2 Executive Summary
3 Tay-Sachs Disease Overview
3.1 Guidelines and Stages
3.2 Pathophysiology
3.3 Screening and Diagnosis
3.4 Treatment Pathway
4 Patient Profile
4.1 Patient Profile Overview
4.2 Patient Psychology and Emotional Impact Factors
4.3 Risk Assessment and Treatment Success Rate
5 Tay-Sachs Disease Epidemiology Analysis - 7MM
5.1 7MM Epidemiology Scenario Overview (2017-2032)
5.2 United States Tay-Sachs Disease Epidemiology Forecast (2017-2032)
5.3 EU-4 and United Kingdom Tay-Sachs Disease Epidemiology Forecast (2017-2032)
5.3.1 Germany Tay-Sachs Disease Epidemiology Forecast (2017-2032)
5.3.2 France Tay-Sachs Disease Epidemiology Forecast (2017-2032)
5.3.3 Italy Tay-Sachs Disease Epidemiology Forecast (2017-2032)
5.3.4 Spain Tay-Sachs Disease Epidemiology Forecast (2017-2032)
5.3.5 United Kingdom Tay-Sachs Disease Epidemiology Forecast (2017-2032)
5.4 Japan Tay-Sachs Disease Epidemiology Forecast (2017-2032)
6 Tay-Sachs Disease Market Overview - 7MM
6.1 Tay-Sachs Disease Market Historical Value (2017-2023)
6.2 Tay-Sachs Disease Market Forecast Value (2024-2032)
7 Tay-Sachs Disease Market Landscape - 7MM
7.1 Tay-Sachs Disease Developers Landscape
7.1.1 Analysis by Year of Establishment
7.1.2 Analysis by Company Size
7.1.3 Analysis by Region
7.2 Tay-Sachs Disease Product Landscape
7.2.1 Analysis by Diseases Type
7.2.2 Analysis by Treatments
7.2.3 Analysis by Route of Administration
8 Tay-Sachs Disease Challenges and Unmet Needs
8.1 Treatment Pathway Challenges
8.2 Compliance and Drop-Out Analysis
8.3 Awareness and Prevention Gaps
9 Cost of Treatment
10 Tay-Sachs Disease Market Dynamics
10.1 Market Drivers and Constraints
10.2 SWOT Analysis
10.3 Porter's Five Forces Model
10.4 Key Demand Indicators
10.5 Key Price Indicators
10.6 Industry Events, Initiatives, and Trends
10.7 Value Chain Analysis
11 Tay-Sachs Disease Market Segmentation - 7MM
11.1 Tay-Sachs Disease Market by Drug Type
11.1.1 Market Overview
11.1.2 Anticonvulsants
11.1.3 Antipsychotic Medications
11.1.4 Others
11.2 Tay-Sachs Disease Market by Type
11.2.1 Market Overview
11.2.2 Infantile Tay - Sachs Disease
11.2.3 Juvenile Tay-Sachs Disease
11.2.4 Late-Onset Tay-Sachs Disease
11.3 Tay-Sachs Disease Market by Treatment
11.3.1 Market Overview
11.3.2 Medication
11.3.3 Respiratory Care
11.3.4 Physical Therapy
11.4 Tay-Sachs Disease Market by Route of Administration
11.4.1 Market Overview
11.4.2 Injectable
11.4.3 Oral
11.4.4 Others
11.5 Tay-Sachs Disease Market by Distribution Channel
11.5.1 Market Overview
11.5.2 Hospital Pharmacies
11.5.3 Retail Pharmacies
11.5.4 Online Pharmacies
11.6 Tay-Sachs Disease Market by End User
11.6.1 Market Overview
11.6.2 Hospitals
11.6.3 Homecare
11.7 Tay-Sachs Disease Market by Region
11.7.1 Market Overview
11.7.2 United States
11.7.3 EU-4 and the United Kingdom
11.7.3.1 Germany
11.7.3.2 France
11.7.3.3 Italy
11.7.3.4 Spain
11.7.3.5 United Kingdom
11.7.4 Japan
12 United States Tay-Sachs Disease Market
12.1 Tay-Sachs Disease Market Historical Value (2017-2023)
12.2 Tay-Sachs Disease Market Forecast Value (2024-2032)
12.3 Tay-Sachs Disease Market by Drug Type
12.4 Tay-Sachs Disease Market by Treatment Type
13 EU-4 and United Kingdom Tay-Sachs Disease Market
13.1 Tay-Sachs Disease Market Historical Value (2017-2023)
13.2 Tay-Sachs Disease Market Forecast Value (2024-2032)
13.3 Germany Tay-Sachs Disease Market Overview
13.3.1 Tay-Sachs Disease Market by Drug Type
13.3.2 Tay-Sachs Disease Market by Treatment Type
13.4 France Tay-Sachs Disease Market Overview
13.4.1 Tay-Sachs Disease Market by Drug Type
13.4.2 Tay-Sachs Disease Market by Treatment Type
13.5 Italy Tay-Sachs Disease Market Overview
13.5.1 Tay-Sachs Disease Market by Drug Type
13.5.2 Tay-Sachs Disease Market by Treatment Type
13.6 Spain Tay-Sachs Disease Market Overview
13.6.1 Tay-Sachs Disease Market by Drug Type
13.6.2 Tay-Sachs Disease Market by Treatment Type
13.7 United Kingdom Tay-Sachs Disease Market Overview
13.7.1 Tay-Sachs Disease Market by Drug Type
13.7.2 Tay-Sachs Disease Market by Treatment Type
14 Japan Tay-Sachs Disease Market
14.1 Tay-Sachs Disease Market Historical Value (2017-2023)
14.2 Tay-Sachs Disease Market Forecast Value (2024-2032)
14.3 Tay-Sachs Disease Market by Drug Type
14.4 Tay-Sachs Disease Market by Treatment Type
15 Patent Analysis
15.1 Analysis by Type of Patent
15.2 Analysis by Publication year
15.3 Analysis by Issuing Authority
15.4 Analysis by Patent Age
15.5 Analysis by CPC Analysis
15.6 Analysis by Patent Valuation
15.7 Analysis by Key Players
16 Grants Analysis
16.1 Analysis by year
16.2 Analysis by Amount Awarded
16.3 Analysis by Issuing Authority
16.4 Analysis by Grant Application
16.5 Analysis by Funding Institute
16.6 Analysis by NIH Departments
16.7 Analysis by Recipient Organization
17 Clinical Trials Analysis
17.1 Analysis by Trial Registration Year
17.2 Analysis by Trial Status
17.3 Analysis by Trial Phase
17.4 Analysis by Therapeutic Area
17.5 Analysis by Geography
18 Funding and Investment Analysis
18.1 Analysis by Funding Instances
18.2 Analysis by Type of Funding
18.3 Analysis by Funding Amount
18.4 Analysis by Leading Players
18.5 Analysis by Leading Investors
18.6 Analysis by Geography
19 Partnership and Collaborations Analysis
19.1 Analysis by Partnership Instances
19.2 Analysis by Type of Partnership
19.3 Analysis by Leading Players
19.4 Analysis by Geography
20 Supplier Landscape
20.1 Recursion Pharmaceuticals, Inc.
20.1.1 Financial Analysis
20.1.2 Product Portfolio
20.1.3 Demographic Reach and Achievements
20.1.4 Mergers and Acquisition
20.1.5 Certifications
20.2 IntraBioInc
20.2.1 Financial Analysis
20.2.2 Product Portfolio
20.2.3 Demographic Reach and Achievements
20.2.4 Mergers and Acquisition
20.2.5 Certifications
20.3 Johnson & Johnson Services
20.3.1 Financial Analysis
20.3.2 Product Portfolio
20.3.3 Demographic Reach and Achievements
20.3.4 Mergers and Acquisition
20.3.5 Certifications
20.4 Axovant Sciences, Inc.
20.4.1 Financial Analysis
20.4.2 Product Portfolio
20.4.3 Demographic Reach and Achievements
20.4.4 Mergers and Acquisition
20.4.5 Certifications
20.5 Pfizer
20.5.1 Financial Analysis
20.5.2 Product Portfolio
20.5.3 Demographic Reach and Achievements
20.5.4 Mergers and Acquisition
20.5.5 Certifications
20.6 Sio Gene Therapies Ltd
20.6.1 Financial Analysis
20.6.2 Product Portfolio
20.6.3 Demographic Reach and Achievements
20.6.4 Mergers and Acquisition
20.6.5 Certifications
20.6.6 F. Hoffmann-La
20.7 Roche Ltd
20.7.1 Financial Analysis
20.7.2 Product Portfolio
20.7.3 Demographic Reach and Achievements
20.7.4 Mergers and Acquisition
20.7.5 Certifications
20.8 Bayer AG
20.8.1 Financial Analysis
20.8.2 Product Portfolio
20.8.3 Demographic Reach and Achievements
20.8.4 Mergers and Acquisition
20.8.5 Certifications
20.9 Bausch Health
20.9.1 Financial Analysis
20.9.2 Product Portfolio
20.9.3 Demographic Reach and Achievements
20.9.4 Mergers and Acquisition
20.9.5 Certifications
20.10 Boehringer Ingelheim International GmbH
20.10.1 Financial Analysis
20.10.1 Product Portfolio
20.10.2 Demographic Reach and Achievements
20.10.3 Mergers and Acquisition
20.10.4 Certifications
21 Tay-Sachs Disease Market - Distribution Model (Additional Insight)
21.1 Overview
21.2 Potential Distributors
21.3 Key Parameters for Distribution Partner Assessment
22 Key Opinion Leaders (KOL) Insights (Additional Insight)
23 Company Competitiveness Analysis (Additional Insight)
23.1 Very Small Companies
23.2 Small Companies
23.3 Mid-Sized Companies
23.4 Large Companies
23.5 Very Large Companies
24 Payment Methods (Additional Insight)
24.1 Government Funded
24.2 Private Insurance
24.3 Out-of-Pocket
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